Original Research Accepted on 27 Mar 2026 RNA Activation as a Precision Dosing Modality: MTL-CEBPA for Controlled Enzyme Elevation in MPS I-H in Gene and Cell Therapy Vikash ReebyeKonstantina Skourti-StathakiKonstantinos VanezisMin-sun SongMichael PrzybillaRose HodgsonKarin PurdieAmelia Julieta TesoneGrazia PizzaSheba Jarvis Frontiers in Medicine 342 views