Review
Published on 30 Apr 2021
Gene Replacement Therapies for Genodermatoses: A Status Quo
in Genetics of Common and Rare Diseases
Frontiers in Genetics
doi 10.3389/fgene.2021.658295
- 9,284 views
- 12 citations
66 articles related to "Gene Replacement"
Articles
Review
Published on 07 Jan 2022
Gene-Based Therapeutics for Inherited Retinal Diseases
in Human and Medical Genomics
Frontiers in Genetics
doi 10.3389/fgene.2021.794805
- 17,624 views
- 57 citations
Review
Published on 14 May 2014
Insights gained from gene therapy in animal models of retGC1 deficiency
in Methods and Model Organisms
Frontiers in Molecular Neuroscience
doi 10.3389/fnmol.2014.00043
- 6,841 views
- 14 citations
Original Research
Published on 24 May 2018
Targeted Deletion of the USTA and UvSLT2 Genes Efficiently in Ustilaginoidea virens With the CRISPR-Cas9 System
in Plant Pathogen Interactions
Frontiers in Plant Science
doi 10.3389/fpls.2018.00699
- 9,991 views
- 105 citations
Review
Published on 05 Jan 2022
Adeno-Associated Virus (AAV)-Mediated Gene Therapy for Duchenne Muscular Dystrophy: The Issue of Transgene Persistence
in Neuromuscular Disorders and Peripheral Neuropathies
Frontiers in Neurology
doi 10.3389/fneur.2021.814174
- 35,987 views
- 73 citations
Review
Published on 20 Oct 2022
Gene regulatory and gene editing tools and their applications for retinal diseases and neuroprotection: From proof-of-concept to clinical trial
in Neuropharmacology
Frontiers in Neuroscience
doi 10.3389/fnins.2022.924917
- 8,277 views
- 10 citations
Mini Review
Published on 26 Sep 2011
Immunity and AAV-Mediated Gene Therapy for Muscular Dystrophies in Large Animal Models and Human Trials
in Microbial Immunology
Frontiers in Microbiology
doi 10.3389/fmicb.2011.00201
- 10,925 views
- 48 citations
Original Research
Published on 25 Mar 2013
Homoeologous GSL-ELONG gene replacement for manipulation of aliphatic glucosinolates in Brassica rapa L. by marker assisted selection
in Plant Genetics and Genomics
Frontiers in Plant Science
doi 10.3389/fpls.2013.00055
- 7,455 views
- 13 citations
Original Research
Published on 14 Jun 2021
Gene Replacement in Arabidopsis Reveals Manganese Transport as an Ancient Feature of Human, Plant and Cyanobacterial UPF0016 Proteins
in Plant Physiology
Frontiers in Plant Science
doi 10.3389/fpls.2021.697848
- 4,697 views
- 6 citations
Original Research
Published on 24 Apr 2026
PEG-mediated transformation: a tool for random integration or targeted gene replacement in Colletotrichum camelliae
in Microbe and Virus Interactions with Plants
Frontiers in Microbiology
doi 10.3389/fmicb.2026.1814272
- 860 views
Original Research
Published on 25 Jul 2017
Gene Replacement and Fluorescent Labeling to Study the Functional Role of Exopolysaccharides in Bifidobacterium animalis subsp. lactis
in Food Microbiology
Frontiers in Microbiology
doi 10.3389/fmicb.2017.01405
- 11,870 views
- 30 citations
Original Research
Published on 24 Mar 2023
Early postnatal administration of an AAV9 gene therapy is safe and efficacious in CLN3 disease
in Genetics of Common and Rare Diseases
Frontiers in Genetics
doi 10.3389/fgene.2023.1118649
- 7,718 views
- 21 citations
Original Research
Published on 04 Apr 2024
TMC function, dysfunction, and restoration in mouse vestibular organs
in Neuro-Otology
Frontiers in Neurology
doi 10.3389/fneur.2024.1356614
- 6,472 views
- 13 citations
Review
Published on 06 Oct 2021
Current and Future Prospects for Gene Therapy for Rare Genetic Diseases Affecting the Brain and Spinal Cord
in Brain Disease Mechanisms
Frontiers in Molecular Neuroscience
doi 10.3389/fnmol.2021.695937
- 47,340 views
- 80 citations
Review
Published on 19 Sep 2011
Innate Immune Responses to AAV Vectors
in Microbial Immunology
Frontiers in Microbiology
doi 10.3389/fmicb.2011.00194
- 26,645 views
- 152 citations
Review
Published on 28 Jan 2021
POLR3-Related Leukodystrophy: Exploring Potential Therapeutic Approaches
in Cellular Neuropathology
Frontiers in Cellular Neuroscience
doi 10.3389/fncel.2020.631802
- 14,908 views
- 18 citations