Genome Editing using AAV Vectors: A Synergistic Approach for Rare Disease Treatment

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Published on 22 Sep 2025

Rewriting the script: gene therapy and genome editing for von Willebrand Disease

Alastair Barraclough
Isabel Bär
Tirsa van Duijl
Karin Fijnvandraat
Jeroen C. J. Eikenboom
Frank W. G. Leebeek
Ruben Bierings
Jan Voorberg
Despoina Trasanidou

doi 10.3389/fgeed.2025.1620438

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Frontiers in Genome Editing

Frontiers in Genome Editing

Genome Editing Tools and Mechanisms

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