Genome Editing using AAV Vectors: A Synergistic Approach for Rare Disease Treatment

Rewriting the Script: Gene Therapy and Genome Editing for Von Willebrand Disease

• Alastair Barraclough
• Isabel Bär
• Tirsa Van Duijl
• Karin Fijnvandraat
• Jeroen C.J. Eikenboom
• Frank W.G. Leebeek
• Ruben Bierings
• Jan Voorberg
• Despoina Trasanidou