Strategic Drug Development for Rare and Underexplored Diseases

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ORIGINAL RESEARCH

Published on 20 Aug 2025

Safety assessment of laronidase: real-world adverse event analysis based on the FDA adverse event reporting system (FAERS)

Zhuomiao Lin
Junling Xue
Meiqing Yang
Xihui Yu
Jiahong Zhong

doi 10.3389/fphar.2025.1623921

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REVIEW

Accepted on 28 Jul 2025

Sickle cell disease: Understanding pathophysiology, clinical features and advances in gene therapy approaches

Muhammad Taher
Aisyah Sofea Aminondin
Nur Asyilah Nasir
Noor Afiqah Jasmadi
Nur Irdeena Nizam
Ilhan Syahmi Bin Shahrul
Deny Susanti
Junaidi Khotib
Muhammad Salahuddin Haris

doi 10.3389/fphar.2025.1630994

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Frontiers in Pharmacology

Frontiers in Pharmacology

Experimental Pharmacology and Drug Discovery

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